Cystic fibrosis transmembrane conductance regulator

Characterizing responses to CFTR-modulating drugs using rectal organoids derived from subjects with cystic fibrosis

Mechanism of CFTR correction by type I folding correctors

Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis

Lentiviral Vectors for the Treatment and Prevention of Cystic Fibrosis Lung Disease

Gene delivery to the lungs: pulmonary gene therapy for cystic fibrosis

Design and characterization of 4D-710, an aerosolized gene therapy for cystic fibrosis lung disease

Design and characterization of 4D-710, an aerosolized gene therapy for cystic fibrosis lung disease